Fulcrum Therapeutics

Risk vs. Reward in Biotech. For Fulcrum, the decision is clear: patients make the potential rewards greater than any risk. Hear from our own Sara Johnson Davis, VP, Head of Patient Advocacy & Policy, in her latest interview with the Milken Institute's Executive Insights series! #ScienceForPatients #Leadership

Empowerment. Strength. Courage. Those three words were more than a theme at SCDAA’s 53rd Annual Convention. They were the energy in every session, every conversation, and every moment. Thank you to SCDAA for bringing the community together for this year’s convention, and to all the speakers who inspired us to keep forging ahead with strength and courage. Sickle Cell Disease Association of America, Inc. — National, Cayenne Wellness Center & Children´s Foundation, Sickle Cell Reproductive Health Education Directive, André Marcel Harris, MSW #SCDAA #Empowerment

Fulcrum Therapeutics is proud to join over 60 rare disease companies urging the immediate restoration of the Rare Pediatric Disease Priority Review Voucher (PRV) Program. This program is a crucial, cost-effective tool that stimulates research and development (R&D) for therapies aimed at rare, often fatal, pediatric diseases. The PRV incentive is vital for attracting investment into the rare disease space, mitigating risk, and ensuring innovators can deliver first-in-class treatments where they are desperately needed. Our CEO, Alex Sapir, signed the joint CEO letter calling for Congress to act swiftly to reauthorize the program. The future of hope for children with rare diseases depends on its restoration. #RareDisease #PediatricHealth #DrugDevelopment #Innovation

We’re thrilled to welcome Lisa Percival as our new Chief Regulatory Officer! With decades of global regulatory experience and a career dedicated to the development of new medicines for high unmet need diseases and expanding access for patients, Lisa brings exceptional leadership and expertise to the FULcrew. Welcome to the team, Lisa! #FULcrew #Leadership #Biotech #RareDisease

Today we honor those who’ve served. At Fulcrum, we also recognize that service can come with unseen challenges, including health risks linked to genetic traits like Sickle Cell Trait (SCT). Service members with SCT face a 24% higher risk of complications during intense physical exertion. It’s a reminder of why lifelong, equitable healthcare for veterans matters and why awareness is key to protecting those who protect us. Thank you to all who have served. Source: Risk of Exertional Heat Illnesses Associated with Sickle Cell Trait in U.S. Military (2019) #VeteransDay #SickleCellAwareness

This September, we honored Sickle Cell Awareness Month. It was a time to listen, learn, and take action alongside the people living this story every day. Over the month, we had the chance to make fresh connections and reconnect in so many meaningful ways. From the Cayenne Wellness Summit to our Sickle Cell Warrior Panel, from community partnerships and walks in Houston and Michigan to our first global patient webinar, we were reminded that awareness is just the beginning. Each moment and each person reminded us that what matters most are the connections that last long after September ends. #SickleCellAwarenessMonth #SickleCellDisease #SickleCellCommunity

Happy Halloween! The FULcrew went all in on this year’s theme: “Dress like your job…but make it exaggerated!” #DressLikeYourJob #CostumeChallenge

This week, our CEO, Alex Sapir, joined fellow leaders from The Rare Disease Company Coalition and the U.S. Food and Drug Administration (FDA), including Commissioner Dr. Martin Makary and CDER Director Dr. George Tidmarsh, at the RDCC–FDA CEO Roundtable on Rare Disease Drug Development. Together, they explored ways to build on the FDA’s strong commitment to accelerate drug development for the rare disease community. We’re grateful to be part of a community working together to turn research into real change for people living with rare diseases. #RareDisease #TogetherForPatients

September marked Sickle Cell Awareness Month, and we came together for Stories of Strength in Sickle Cell Disease. Thank you to Hanif Mouehla, Simone Eastman Uwan M.D., Nola Juste, MPH, CCRP, and Derek Robertson, MBA, JD, CHC for sharing powerful perspectives as warriors, caregivers, and advocates. Your voices remind us that change begins with listening and grows through action. #SickleCellAwarenessMonth #AdvocacyInAction #CommunityVoices

Oktoberfest, Fulcrum-style! 🥨 Our team came together for a little Oktoberfest fun, complete with pretzels, beer sampling, and plenty of good cheer.